Rocket Pharma focuses on developing gene therapy treatments for rare, undertreated diseases, including Fanconi Anemia, Pyruvate Kinase Deficiency, Leukocyte Adhesion Deficiency-1, and Infantile Malignant Osteopetrosis. They also have a program for an undisclosed rare pediatric disease. The company values its team members and offers competitive compensation packages and excellent health benefits. Rocket Pharma is recognized as a leading biotechnology innovator and aims to make a difference for patients in need.